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RARE DISEASE CENTER OF EXCELLENCE

There is nothing like rare disease research

Biorasi optimizes speed, agility, and quality for rare disease clinical studies – building strategies that integrate the patient’s journey with our partners’ goals.

Nilufer Celenk, VP, Pricing and Strategic Partnerships

Every clinical trial presents challenges, no matter the therapeutic area. But rare disease trials are especially difficult due to the sparsity of the patient population, knowledge gaps in the research community, and a lack of study funding, among other difficulties.

These obstacles are why rare disease trials are almost

70% more likely

than other trials to face a major delay.

Speed and agility make the difference

Rare Disease

Speed and agility make the difference

The good news: Although rare disease clinical trials have their own specific requirements, they share a common set of challenges. At Biorasi’s Rare Disease Center of Excellence, we set out to solve those challenges and deliver successful rare disease clinical trials on time.

Rare Disease

Fast, responsive, and flexible

Rare Disease

Fast, responsive, and flexible

Over nearly 20 years, Biorasi has meticulously built a team and operating model with the capability to keep your study moving rapidly. And nowhere is that distinction more important than in rare diseases.

Rare Disease

Rare Disease Center of Excellence

 

Led by Marc Gas, PhD, Biorasi’s Rare Disease Center of Excellence features clinical and operational expertise backed by our own Scientific Advisory Board of industry experts and KOLs. When you choose Biorasi as your CRO, you are choosing an industry leader that meets your rare disease clinical trial goals successfully.

DERMATOLOGY RARE DISEASES

  • Generalized Pustular Psoriasis (GPP)
  • Palmoplantar Pustulosis (PPP)
  • Xeroderma Pigmentosum (XP)

GASTROENTEROLOGY RARE DISEASES

  • Eosinophilic Esophagitis (EoE)

GENETIC RARE DISEASES

  • Mucopolysaccharidosis Type II (MPS II)

HEMATOLOGICAL RARE DISEASES

  • Hereditary Hemorrhagic Telangiectasia (HHT)
  • Paroxysmal Nocturnal Hemoglobinuria (PNH)
  • Thalassemia

INFECTIOUS RARE DISEASES

  • Hepatitis D Virus

NEPHROLOGY RARE DISEASES

  • Calciphylaxis/Calcific Uremic Arteriolopathy (CUA)
  • Complement 3 Glomerulopathy (C3G)
  • Focal Segmental Glomerulosclerosis (FSGS)
  • Immunoglobulin A (IgA) Nephropathy
  • Lupus Nephritis (LN)

NEUROLOGY RARE DISEASES

  • Amyotrophic Lateral Sclerosis (ALS)
  • Friedreich’s Ataxia (FRDA)
  • Multiple Sclerosis (MS)

RARE CANCERS

  • Biliary Tract Cancer
  • Glioblastoma (GBM)
  • Multiple Myeloma (MM)
  • Renal Cell Carcinoma (RCC)

OPHTHALMOLOGY RARE DISEASES

  • Noninfectious Uveitis (NIU)
  • Pediatric Cataracts

RESPIRATORY RARE DISEASES

  • Autoimmune Pulmonary Alveolar Proteinosis (aPAP)
  • Nontuberculosis Mycobacterium Infection (NTM)
  • Cystic Fibrosis (CF)
  • Idiopathic Pulmonary Fibrosis (IPF)

OTHER DISEASES

  • COVID-19